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• n  a congenital disease affecting T cells that can result from a mutation in any one of several different genes; children with it are susceptible to infectious disease; if untreated it is lethal within the first year or two of life

• severe combined immunodeficiency
• SCID

News & Articles

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• Promising thereapy for 'bubble boy' disease
  Scientists now report that 8 out of 9 young children given gene therapy for a type of severe combined immunodeficiency disease, called SCID-X1, are alive and living amid the everyday microbial threats that would otherwise have killed them. The oldest is just over 3 years old.
  Dec. 7, 2013 - Minnesota Public Radio
• Gene Therapy Keeps 'Bubble Boy' Disease At Bay In 8 Children
  Researchers say they are achieving success in curing the genetic defect that causes some children to be born without immune defenses, a rare condition made famous in the 1970s by a Texas boy who lived most of his short life in a sterile "bubble." Scientists now report that 8 out of 9 young children given gene therapy for a type of severe combined immunodeficiency disease, called SCID-X1 , are ...
  Dec. 7, 2013 - KERA North Texas